Finding a new medicine is never easy. But developing treatments for patients with rare diseases — conditions that afflict fewer than 200,000 people in the United States — is particularly challenging.

The process of discovering new drugs is mainly linear—and prone to bottlenecks. Putting a new drug on the pharmacy shelf may take well over a decade, which spells a waste of time and money if the drug ...

Developing high-quality, safe, and effective drugs is a complex process that requires varied scientific skills and stringent regulatory assessments. Drug development is a process that spans many years ...