Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
All muscular dystrophies cause muscle weakness, but life expectancy can vary dramatically between types of muscular dystrophy.
Disability advocate TaLisha Gryzb is a mother of four living with muscular dystrophy who educates viewers about her ...
Sarepta’s blockbuster gene therapy has come under scrutiny following a string of patient deaths.
Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for a progressive muscle‑wasting disorder showed sustained benefit in ...
"Muscular dystrophy can take many things from me, but it will not take away my happiness, nor will it take away my faith." ...
In his CEO Commentary, Frederic Revah, Ph.D., underscores the dedication, expertise and successes of Genethon's 240 scientists and professional staff as they pursue new gene therapy treatments for ...
"High clinical suspicion is important for this population of patients. Since muscular dystrophy is progressive in nature, monitoring disease progression in these patients is critical for timing ...
In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...
Researchers at Kumamoto University have demonstrated that iron supplementation can significantly alleviate muscle pathology ...
By Mariam Sunny Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for Duchenne muscular dystrophy slowed disease ...
While it’s established that Duchenne muscular dystrophy (DMD) causes a loss of muscle mass and strength, few studies have examined the gastrointestinal issues tied to DMD. Initial fractures are the ...