12 Pros and Cons of Gene Therapy

Adeno-Associate Virus (AAV) for Gene Therapy | AskBio

Gene Therapy Types

Ex Vivo & In Vivo Gene Therapy Techniques

In a major leap for gene therapy, scientists have developed a way to reactivate silenced genes without the risks associated with breaking DNA strands. This new "epigenetic editing" technique uses a modified CRISPR system to remove tiny chemical tags, methyl groups that act as molecular anchors, keeping specific genes switched off. The researchers confirmed that these tags aren't just byproducts; they actively silence genes. By "brushing off" these anchors, they were able to turn genes back on in

New gene therapy for Duchenne muscular dystrophy offers hope - UW Medicine | Newsroom

Growing success in new gene therapy for inherited deafness— Harvard Gazette